Treating Hemophilia

While hemophilia cannot be cured, it can be treated and successfully managed. Hemophilia A is treated by increasing the level of factor VIII (FVIII) in the blood. This is done by an infusion (injection) of factor replacement therapy, also called FVIII product.

Initially, infusion is typically done at a hospital or hemophilia treatment center (HTC), but parents usually learn how to infuse their children themselves. Infusing at home is convenient and saves time (which is especially important to minimizing joint damage when joint bleeds occur). Eventually, when children are older, they learn to infuse themselves.

Inhibitors

Up to 36% of patients with severe hemophilia A will develop an inhibitor in response to treatment. If the clotting factor is seen as a foreign invader, the body develops the inhibitor to block the clotting action of the factor. This makes treatment more challenging. Please consult with your physician or HTC if you have questions about inhibitors.

Types of factor

There are two kinds of FVIII products: human plasma-derived and recombinant FVIII. Human plasma-derived products are taken directly from donated plasma. With recombinant factor, the proteins needed to make FVIII product are not taken from human plasma, but synthesized in a laboratory using recombinant DNA technology.